Interventions of Interest

  • apitegromab (Scholar Rock Holdings)
  • nusinersen (Spinraza®, Biogen)
  • onasemnogene abeparvovec-xioi (Zolgensma®, Novartis)
  • risdiplam (Evrysdi®, Genentech)

For questions please contact info@icer.org.

View the Key Stakeholder List.