Interventions of Interest

      • apitegromab (Scholar Rock Holdings)
      • nusinersen (Spinraza®, Biogen)
      • onasemnogene abeparvovec-xioi (Zolgensma®, Novartis)
      • risdiplam (Evrysdi®, Genentech)

      For questions please contact Temiwunmi Shobanke, Program Manager, tshobanke@icer.org

      View the Key Stakeholder List.