Topic: Policy: Gene Therapies

Managing the Challenges of Paying for Gene Therapies

Apr 2024 | Policy Paper

ICER and NEWDIGS at Tufts Medical Center released a white paper on the challenges and potential policy options for paying for gene therapies. The report analyzes the intersecting challenges of ensuring patient access for gene therapies, including determining fair prices, managing clinical uncertainty, and mitigating financial shocks.  This paper draws upon the body of work […]

Gene Therapy: Understanding the Science, Assessing the Evidence, and Paying for Value 

Dec 2016 | Policy Paper

This white paper was developed following a December 2016 meeting of ICER’s membership program, during which leaders from 20 payer and manufacturer organizations convened to share their perspectives on the future of gene therapy. The paper explores the scientific frontier being opened up by emerging gene therapies, with the potential for curing or substantially improving the […]